Vimizim
Chemical Name | elosulfase alfa |
Dosage Form | Injection (intravenous; 5 mg/5 mL (1 mg/mL)) |
Drug Class | Enzymes |
System | Musculoskeletal |
Company | BioMarin |
Approval Year | 2014 |
Indication
- Treatment for Mucopolysaccharidosis type IVA (Morquio A syndrome).