Kanuma
Chemical Name | sebelipase alfa |
Dosage Form | Injection (intravenous; 20 mg/10 mL) |
Drug Class | Enzymes |
System | Digestive, Cardiovascular, Blood |
Company | Alexion Pharmaceuticals Inc. |
Approval Year | 2015 |
Indication
- To treat patients with a rare disease known as lysosomal acid lipase (LAL) deficiency.