Galafold
Chemical Name | migalastat |
Dosage Form | Capsules (oral; 123 mg) |
Drug Class | Miscellaneous |
System | Digestive, Urinary, Cardiovascular, Skin |
Company | Amicus Therapeutics |
Approval Year | 2018 |
Indication
- To treat Fabry disease in adults with an amenable galactosidase alpha gene.