Vyondys 53

Chemical Namegolodirsen
Dosage FormInjectable (intravenous; 50 mg/mL)
Drug ClassOligonucleotides
SystemMusculoskeletal
CompanySarepta Therapeutics Inc.
Approval Year2019

Indication

  • Vyondys 53 is indicated for the treatment of Duchenne muscular dystrophy (DMD) in patients who have a confirmed mutation of the DMD gene that is amenable to exon 53 skipping.
Last updated on 10/27/2020

More on this drug: Clinical Trials

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Document TitleYearSource
Vyondys 53 (golodirsen) Prescribing Information2019Sarepta Therapeutics